SMA Gene Therapy

Gene TherapyAs you all know most of our fundraising lately has been going to the amazing Gene Therapy program for SMA coming out of OSU/Nationwides childrens hospital…..we were so honored when one of the researchers, Dr. Brian Kasper asked to meet our family and especially Sophia. Dr. Kasper was in NY last week for a conference at Columbia and was so generous to spend some time with us on thursday. He was also very gracious to agree to do a video recorded Q/A session…..we asked the SMA community to submit questions and we recorded the answers!!!! It was such a positive experience, to view the recordings with Dr. Kasper please visit our YouTube Channel “Sophiascure”


  1. Thank you for your work, Dr. Kaspar!

Leave a Reply to Getty Owl Cancel reply


© 2011 The Sophia's Cure Foundation. All Rights Reserved. The Sophia's Cure Foundation is a non-profit 501(c)(3) public charity. Site by modSpot