First child with Spinal Muscular Atrophy has been injected with AAV9 Gene Therapy..

We are proud to announce that the first child in the Gene Therapy Program was injected just over 30 days ago. Sophia’s Cure Foundation was present for this monumental day. We are looking forward to more children receiving this treatment in the near future. Thank you to Nationwide and AveXis !! We were so honored to watch history in the making, 5 years of emotions came to a head at the moment we heard “its done” Vinny and I both looked at each other and burst into uncontrollable tears……tears of joy for all the hard work, tears of sadness for the SMA children lost, tears of hope for the future……. Here we are on the flight home just 3 hours after the injection, a day that will live in our hearts forever…Thank you for your support and love!!!

About Catherine Gaynor

Mom to beautiful Sophia.... SMA Type 1

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