Archives for August 2013


August is SMA Awareness month and do we have some great news to celebrate the occasion. Let the countdown begin!*** Here is a picture of hard work. This is the paper work of a program with the best pre-clinical data ever in SMA. Thousands of pages outlining results, clinical trial design and safety for Dr. Kaspar's Systemic Delivery of the AAV9/SMN Gene Therapy Program for SMA. The best has officially been received by The Food and Drug Administration. They have 30 days … [Read more...]

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